Keyword

Critical Review

5 Publications

JOSHA’S CRITICAL REVIEW OF “Efficacy of Larotrectinib in TRK Fusion– Positive Cancers in Adults and Children”
Life Sciences
| DOI: 10.17160/josha.5.4.427

JOSHA’S CRITICAL REVIEW OF “Efficacy of Larotrectinib in TRK Fusion– Positive Cancers in Adults and Children”

R

Roland Mertelsmann, Gerhard G. Steinmann

Albert-Ludwigs Universität

JOSHA´S CONCLUSION. IMPORTANT PROGRESS; ESPECIALLY FOR PATIENTS WITH SARCOMAS FOR WHOM VERY FEW TREATMENT ALTERNATIVES EXIST. TRK-FUSION TESTING SHOULD BECOME ROUTINE IN PATIENTS WITH SARCOMA AND SELECTED PATIENTS WITH OTHER…

1,661
3,315
JOSHA’S CRITICAL REVIEW OF “GENE THERAPY IN PATIENTS WITH TRANSFUSION-DEPENDENT β-THALASSEMIA” BY A.A. Thompson et al. N Engl J Med 2018; 378:1479- 1493.
Life Sciences
| DOI: 10.17160/josha.5.4.426

JOSHA’S CRITICAL REVIEW OF “GENE THERAPY IN PATIENTS WITH TRANSFUSION-DEPENDENT β-THALASSEMIA” BY A.A. Thompson et al. N Engl J Med 2018; 378:1479- 1493.

R

Roland Mertelsmann, Gerhard Steinmann

Albert-Ludwigs Universität

THESE INTERIM RESULTS OF TWO PHASE I/II TRIALS ARE REMARKABLE. THOMPSON AND COLLEAGUES DEMONSTRATE THE PROGRESS OF CLINICAL GENE THERAPY FOR MONOGENETIC DISEASES WITH A MEDIAN OBSERVATION TIME OF 26…

1,663
3,285